Optimized ASO chemistry significantly improves Ush1c gene splicing and visual function in Ush1c-216AA mice

Document Type

Conference Proceeding

Publication Date

6-1-2024

Publication Title

Investigative Ophthalmology and Visual Science

Abstract

Association for Research in Vision and Ophthalmology Annual Meeting, ARVO 2024, May 5 - 9, 2024, Seattle, WA

First Page

2194

Volume

65

Issue

7

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