Efficacy and safety of long-acting cabotegravir compared with daily oral tenofovir disoproxil fumarate plus emtricitabine to prevent HIV infection in cisgender men and transgender women who have sex with men 1 year after study unblinding: a secondary analysis of the phase 2b and 3 HPTN 083 randomised controlled trial

Authors

Raphael J. Landovitz, David Geffen School of Medicine at UCLA
Brett S. Hanscom, Fred Hutchinson Cancer Center
Meredith E. Clement, LSU Health Sciences Center - New OrleansFollow
Ha V. Tran, The University of North Carolina at Chapel Hill
Esper G. Kallas, Universidade de São Paulo
Manya Magnus, Milken Institute School of Public Health
Omar Sued, Fundacion Huesped
Jorge Sanchez, Centro de Investigaciones Tecnológicas, Biomédicas y Medioambientales
Hyman Scott, San Francisco Department of Public Health
Joe J. Eron, The University of North Carolina at Chapel Hill
Carlos del Rio, Emory University School of Medicine
Sheldon D. Fields, Pennsylvania State University
Mark A. Marzinke, Johns Hopkins School of Medicine
Susan H. Eshleman, Johns Hopkins School of Medicine
Deborah Donnell, Fred Hutchinson Cancer Center
Matthew A. Spinelli, University of California, San Francisco
Ryan M. Kofron, David Geffen School of Medicine at UCLA
Richard Berman, Fred Hutchinson Cancer Center
Estelle M. Piwowar-Manning, Johns Hopkins School of Medicine
Paul A. Richardson, Johns Hopkins School of Medicine
Philip A. Sullivan, Johns Hopkins School of Medicine
Jonathan P. Lucas, FHI 360
Peter L. Anderson, University of Colorado Anschutz Medical Campus
Craig W. Hendrix, Johns Hopkins School of Medicine
Adeola Adeyeye, National Institute of Allergy and Infectious Diseases (NIAID)
James F. Rooney, Gilead Sciences Incorporated
Alex R. Rinehart, ViiV Healthcare
Myron S. Cohen, The University of North Carolina at Chapel Hill

Document Type

Article

Publication Date

12-1-2023

Publication Title

The Lancet HIV

Abstract

Background: Injectable cabotegravir was superior to daily oral tenofovir disoproxil fumarate plus emtricitabine for HIV prevention in two clinical trials. Both trials had the primary aim of establishing the HIV prevention efficacy of long-acting injectable cabotegravir pre-exposure prophylaxis (PrEP) compared with tenofovir disoproxil fumarate plus emtricitabine daily oral PrEP. Long-acting PrEP was associated with diagnostic delays and integrase strand-transfer inhibitor (INSTI) resistance. This report presents findings from the first unblinded year of the HIV Prevention Trials Network (HPTN) 083 study. Methods: The HPTN 083 randomised controlled trial enrolled HIV-uninfected cisgender men and transgender women at elevated HIV risk who have sex with men, from 43 clinical research sites in Africa, Asia, Latin America, and the USA. Inclusion criteria included: a negative HIV serological test at the screening and study entry, undetectable HIV RNA levels within 14 days of study entry, age 18 years or older, overall good health as determined by clinical and laboratory evaluations, and a creatinine clearance of 60 mL/min or higher. Participants were randomly allocated to receive long-acting injectable cabotegravir or daily oral tenofovir disoproxil fumarate plus emtricitabine PrEP. After study unblinding, participants remained on their original regimen awaiting an extension study. HIV infections were characterised retrospectively at a central laboratory. Here we report the secondary analysis of efficacy and safety for the first unblinded year. The primary outcome was incident HIV infection. Efficacy analyses were done on the modified intention-to-treat population using a Cox regression model. Adverse events were compared across treatment groups and time periods (blinded vs unblinded). This trial is registered with ClinicalTrials.gov, NCT02720094. Findings: Of the 4488 participants who contributed person-time to the blinded analysis, 3290 contributed person-time to the first unblinded year analysis between May 15, 2020, and May 14, 2021. Updated HIV incidence in the blinded phase was 0·41 per 100 person-years for long-acting injectable cabotegravir PrEP and 1·29 per 100 person-years for daily oral tenofovir disoproxil fumarate plus emtricitabine PrEP (hazard ratio [HR] 0·31 [95% CI 0·17–0·58], p=0·0003). HIV incidence in the first unblinded year was 0·82 per 100 person-years for long-acting PrEP and 2·27 per 100 person-years for daily oral PrEP (HR 0·35 [0·18–0·69], p=0·002). Adherence to both study products decreased after study unblinding. Additional infections in the long-acting PrEP group included two with on-time injections; three with one or more delayed injections; two detected with long-acting PrEP reinitiation; and 11 more than 6 months after their last injection. Infection within 6 months of cabotegravir exposure was associated with diagnostic delays and INSTI resistance. Adverse events were generally consistent with previous reports; incident hypertension in the long-acting PrEP group requires further investigation. Interpretation: Long-acting injectable cabotegravir PrEP retained high efficacy for HIV prevention in men and transgender women who have sex with men during the first year of open-label follow-up, with a near-identical HR for HIV risk reduction between long-acting injectable cabotegravir and daily oral tenofovir disoproxil fumarate plus emtricitabine PrEP during the first year after unblinding compared with the blinded period. Extended follow-up further defined the risk period for diagnostic delays and emergence of INSTI resistance. Funding: Division of AIDS at the National Institute of Allergy and Infectious Diseases, ViiV Healthcare, and Gilead Sciences.

First Page

e767

Last Page

e778

PubMed ID

37952550

Volume

10

Issue

12

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