Multi-Year Registry Study of Elapegademase-lvlr Treatment in Patients with Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy (ERT)

Authors

Morna Dorsey, University of California, San Francisco
Manish Butte, University of California Los Angeles
Jay Lieberman, The University of Tennessee Health Science Center, Memphis, TN
Heather Lehman, University at Buffalo, State University of New York
Tracy Fausnight, Penn State Health Hershey Medical Center, Hershey, PA
Michael Keller, Children's National Hospital, Washington, DC
Caroline Fradette, Chiesi Global Rare Diseases, Toronto, ON, Canada
Michael Hershfield, Duke University School of Medicine, Durham, NC
Tamara Pozos, Children's Minnesota, Minneapolis, MN
Anna Rozova, Chiesi Global Rare Diseases, Toronto, ON, Canada
Luke Wall, LSU Health Sciences Center - New OrleansFollow
M. Teresa de la Morena, University of Washington and Seattle Children's Hospital, Seattle, WA
Jeffrey Bednarski, Washington University School of Medicine, St. Louis, MO
Teresa Tarrant, Duke University, Durham, NC
Hey Chong, UPMC Children's Hospital of Pittsburgh, PA,
Bob Geng, University of California San Diego, School of Medicine, CA
Noemi Toiber Temin, Chiesi Global Rare Diseases, Toronto, ON, Canada
Susan Laubach, University of California San Diego, School of Medicine, CA
Leo Lin, Chiesi Global Rare Diseases, Toronto, ON, Canada
Talal Mousallem, Duke University Medical Center
Jolan Walter, University of South Florida, Tampa, FL

Document Type

Conference Proceeding

Publication Date

4-23-2024

Publication Title

Clinical Immunology

Abstract

2024 Clinical Immunology Society Annual Meeting: Immune Deficiency and Dysregulation North American Conference, May 1 - 4, 2024, Minneapolis, MN

Volume

262

Issue

Supplement

Comments

Abstract Number 20

Recommended Citation

Dorsey, Morna; Butte, Manish; Lieberman, Jay; Lehman, Heather; Fausnight, Tracy; Keller, Michael; Fradette, Caroline; Hershfield, Michael; Pozos, Tamara; Rozova, Anna; Wall, Luke; de la Morena, M. Teresa; Bednarski, Jeffrey; Tarrant, Teresa; Chong, Hey; Geng, Bob; Temin, Noemi Toiber; Laubach, Susan; Lin, Leo; Mousallem, Talal; and Walter, Jolan, "Multi-Year Registry Study of Elapegademase-lvlr Treatment in Patients with Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy (ERT)" (2024). School of Medicine Faculty Publications. 2904.
https://digitalscholar.lsuhsc.edu/som_facpubs/2904
10.1016/j.clim.2024.109962